Sarepta Therapeutics, Inc. is a biotechnology company focused on developing precision genetic medicines for rare diseases. The company engages in the research, development, and commercialization of gene therapies, aiming to shorten the time from laboratory discoveries to patient access. Sarepta operates in the rare disease therapeutic area, with a commitment to leveraging advanced scientific methods to create effective treatments. Its operations include building gene therapy manufacturing capacity and exploring various diseases and treatment modalities.